[treyd]

Drug has only been tested in mice.

Of course, in this case the issue seems like it's caused by a general deficiency of single protein, maybe that's a good sign for adapting the treatment to humans.

[slibhb]

While the protein was tested in mice, it seems that it was identified by looking at human spinal fluid.

[vercaemert]

Yes. Not a drug in the typical sense. Simply replacing the protein in which the mice are deficient (that was identified by measuring levels in human spinal fluid).

[dang]

Inmiced above. Thanks!