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by tim333 330 days ago
They've managed to treat sickle cell.

>CRISPR/Cas9 can be directed to cut DNA in targeted areas, enabling the ability to accurately edit (remove, add, or replace) DNA where it was cut. The modified blood stem cells are transplanted back into the patient where they engraft (attach and multiply) within the bone marrow...

https://www.fda.gov/news-events/press-announcements/fda-appr...

1 comments

They did it by killing all the normal blood stem cells in the body. This is difficult to say the least for something that is completely systemic