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by herlitzj
1212 days ago
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https://www.thelancet.com/journals/lancet/article/PIIS0140-6... This paper seems to have more details on the actual procedure Patients were treated and monitored according to the schedule described in the appendix (p 17) and as previously reported.16, 17 HSPCs harvested from bone marrow or mobilised peripheral blood (MPB) were transduced with clinical-grade lentiviral vector encoding human ARSA cDNA under the control of the human phosphoglycerate kinase gene promoter. |
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